Publications

Targeting Chronic Anemia in Thalassemia: The Emerging Role of Mitapivat as a Disease-Modifying Therapy Kevin H.M. Kuo, MD, MSc, FRCPCAssociate ProfessorDivision of Hematology, Department of Medicine, Faculty of Medicine, University of TorontoInstitute of Health Policy, Management and Evaluation, Dalla Lana School of Public Health, University of Toronto   This article…

Highlights and Concerns in Thrombotic thrombocytopenic purpura TTP Treatment: From Pathophysiology to the Era of Caplacizumab Raimondo De Cristofaro, Associate Professor of Internal Medicine, Faculty of Medicine and Surgery “A. Gemelli”, Università Cattolica del Sacro Cuore (Rome, Italy)   This article is part of the Garden Experts Insights series, featuring…

Rethinking Evidence in Hemophilia Care: A Critical Analysis of International Consensus Guidelines Cedric Hermans, MD, PhD, FRCP(Lon, Edin)Full Professor, Head Haemostasis and Thrombosis UnitHaemophilia Clinic Division of Adult Haematology St-Luc University Hospital (Brussels), Vice-President Medical of the WFH Continuing our editorial series featuring insights from leading experts participating in GARDEN…

Extended Half-Life Therapies: What Real-World Practice Shows Mariasanta Napolitano, MD, PhD PROMISE Department, University of Palermo, Palermo, Italy Haematology and Rare Disease Unit, “V. Cervello” Hospital, Palermo, Italy This article opens a series of contributions featuring insights from speakers at our ECM webinars, now presented as editorial content. We begin…

🌐 Cell and Gene Therapies: New Perspectives on Access to Innovative Treatments 🌐 📜 Today, we’re sharing one of the latest publications from the New England Journal of Medicine, exploring the new access model for cell and gene therapies for Medicare and Medicaid beneficiaries. This is a crucial topic for…